RARECast
A podcast by RARECast - Thursdays
548 Episodes
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A Heart Attack that Led to a Rare Disease Diagnosis
Published: 30/01/2025 -
Targeting Rare Liver Diseases with Gene Editing Therapies
Published: 23/01/2025 -
Using AI to De-Risk Rare Disease Drug Development
Published: 16/01/2025 -
Addressing a Growing Demand for Plasma-Derived Therapies
Published: 09/01/2025 -
Empowering Patients with Data to Drive Drug Development
Published: 02/01/2025 -
How Advocates Are Advancing a Treatment for an Ultra-Rare Disease
Published: 26/12/2024 -
Engineering B Cells to Produce Therapeutic Proteins
Published: 19/12/2024 -
A Pipeline Win as BridgeBio Learns to Balance Theory with Practice
Published: 12/12/2024 -
Considering What It Will Take for Payers to Embrace Advances in Sequencing
Published: 05/12/2024 -
Finding Strength
Published: 27/11/2024 -
A Non-Profit Works to Advance a DMD Gene Therapy
Published: 21/11/2024 -
Accepting What We Can’t Understand
Published: 14/11/2024 -
A Gene Therapy Company Born from a Father’s Efforts to Save his Daughter
Published: 07/11/2024 -
Lowering Barriers to Clinical Trial Participation with Do-It-Yourself Blood Sample Collection
Published: 31/10/2024 -
Scaling N-of-1 Therapies to Viability
Published: 24/10/2024 -
Building Gene Therapies that Address Gain and Loss of Function Simultaneously
Published: 17/10/2024 -
How One Woman Climbed from Patient to Advocate
Published: 10/10/2024 -
Shortening the Diagnostic Odyssey
Published: 03/10/2024 -
Making Exomes More Revealing
Published: 26/09/2024 -
How One Patient Organization Catalyzed Drug Development
Published: 19/09/2024
RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.
